Curative Therapy of Sickle Cell Disease Using Gene Editing Technologies
Nand Lal & Priya Prajapati · Asian Journal of Biotechnology and Genetic Engineering · 2023
Sickle cell disease (SCD) is a monogenic blood disorder caused by a single nucleotide mutation in the β-globin gene that swaps the hydrophilic glutamic acid at position six with the hydrophobic valine. Haematopoietic stem cell transplantation is the only curative treatment for SC...
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Research Article