A Critical Appraisal of Clinical Practice Guidelines for Pharmacological Treatments of Paroxysmal Nocturnal Hemoglobinuria
Yara Maria da Silva Pires, Flávia Deffert, Thais Humenhuk, Ana Paula Oliveira Vilela, Aline de Fátima Bonetti & Astrid Wiens · Journal of Advances in Biology & Biotechnology · 2023
Aims: Paroxysmal nocturnal hemoglobinuria (PNH) is a rare chronic disease characterized by complement-mediated hemolysis, thrombosis, and bone marrow failure. This study aims to identify methodological limitations in Clinical Practice Guidelines (CPG) for the treatment of PNH. Th...
Open access
Research Article
10.9734/jabb/2023/v26i12668